A Pennsylvania baby is the first to successfully receive personalized gene therapy Doctors used the gene editing tool CRISPR to treat an infant born with a rare and dangerous disease. Scientists ...

Baby KJ Muldoon, the first patient to successfully receive personalized CRISPR gene editing therapy has returned home after ...

In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to successfully receive a personalized CRISPR gene editing therapy. The ...

Infant with rare, incurable disease is first to successfully receive personalized gene therapy treatment. ScienceDaily . Retrieved June 11, 2025 from www.sciencedaily.com / releases / 2025 / 05 ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has been challenging.

A Pennsylvania baby with a rare genetic condition has been successfully treated with a tailor-made therapy using gene-editing technology partly developed by a Vancouver-based company, raising ...

The world’s first patient to successfully receive a CRISPR gene-editing treatment was discharged from Children’s Hospital of Philadelphia on June 2, ABC News reported.  KJ Muldoon, a 10-month-old who ...

The baby, KJ Muldoon of Clifton Heights, Pennsylvania, is one of 350 million people worldwide with rare diseases, most of which are genetic. He was diagnosed shortly after birth with severe CPS1 ...

Personalized CRISPR treatment used on baby with genetic disease by Steph Whiteside - 05/15/25 4:15 PM ET The baby's disease prevented the liver from removing ammonia ...

A research team supported by the National Institutes of Health (NIH) has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable ...

They corrected a specific gene mutation in the baby’s liver cells that led to the disorder. CRISPR is an advanced gene editing technology that enables precise changes to DNA inside living cells. This ...